On The Path
To a Cure

Your donation fuels 
the breakthrough





Meet Walther








Pioneering gene therapy research for Lowe Syndrome









Focused 
on a cure
At the Cure Lowe Foundation, we're laser-focused on developing a breakthrough gene therapy to address the root cause of Lowe syndrome. Every donation is carefully directed toward our core mission: delivering a functional copy of the OCRL gene to halt or even reverse disease progression. Your support directly funds critical research and development, accelerating our mission to transform the future for those affected by this devastating rare disorder.








Lowe Syndrome;

A Multiorgan Challenge

   Lowe syndrome is a devastating rare genetic disorder that primarily affects young boys. Caused by mutations in the OCRL gene, this condition creates life-altering challenges:

   Vision problems that can lead to blindness
   Neurological complications affecting development
   Severe kidney dysfunction requiring constant care
Currently, families face an uphill battle: available treatments only manage symptoms without addressing the root cause. Each day brings new challenges for these brave children and their dedicated families.

But there's hope on the horizon. Through groundbreaking gene therapy research, we're working to not just treat symptoms, but to transform lives. With your support, we can turn this hope into reality.






Our scientific team is unmatched in expertise




 
Dr.  Siyu  Chen  working in the lab 








The Cure Lowe Foundation brings together a world-class team of scientists, industry experts, and patient advocates. Combined our trusted experts have developed several gene therapies and brings decades of research in Lowe Syndrome.




Want to be part of the solution?